Gene therapy is a branch of medicine that focuses on genetically altering cells to generate a therapeutic effect or heal illness by repairing or rebuilding faulty genetic material. Gene therapy is based on the idea of correcting a genetic issue at its source. When a mutation in a gene causes the creation of a defective protein in a hereditary illness, gene therapy might be used to deliver a copy of the gene that does not include the harmful mutation, resulting in the synthesis of a functional protein. This treatment method is known as gene replacement therapy, and it is used to treat hereditary retinal disorders.
